CRISPR Base Editing for a Monogenic Liver Disorder: Off-Target Assessment and Long-Term Follow-Up Obligations. Translational Medicine & Therapeutics Journal, [S. l.], v. 3, n. 2, p. 74–82, 2024. DOI: 10.5281/zenodo.22649285. Disponível em: https://inkwise.org/index.php/TMTJ/article/view/98. Acesso em: 5 nov. 2026.